Guest: Jerry Mendell, MD, is Director of the Center for Gene Therapy in The Research Institute,...
14:43
Guest: Jerry Mendell, MD, is Director of the Center for Gene Therapy in The Research Institute,...
14:43
Dr. Kevin Flanigan Discusses IRES-Induced Dystrophin as a Potential Therapy for DMD
Guest Host: Scott Harper, PhD, is a principal investigator in the Center for Gene Therapy in The...
24:24
Guest: Louise Rodino-Klapac, PhD, is a principal investigator in the Center for Gene Therapy in...
12:40
Dr. Scott Harper Discusses RNAi silencing in Limb Girdle Muscular Dystrophy 1A
Guest: Scott Harper, PhD, is a principal investigator in the Center for Gene Therapy in The...
16:33
Dr. Brian Kaspar Discusses a New Method for Studying ALS, with Potential to Test Therapeutics in...
20:44
Dr. Louis Chicoine Discusses the Effect of Plasmapheresis in Removal of AAV Antibodies for Gene...
11:20
Dr. Volker Straub Discusses the Use of Muscle MRI in Muscular Dystrophy
Dr. Volker Straub Discusses the Use of Muscle MRI in Muscular Dystrophy Guest: Volker Straub,...
19:07
Dr. Jeff Chamberlain Discusses Gene and Cell Mediated Therapies for Muscular Dystrophy
Dr. Jeff Chamberlain Discusses Gene and Cell Mediated Therapies for Muscular Dystrophy Guest:...
31:08
Dr. Paul Martin Discusses Galgt2 Gene Therapy for Muscular Dystrophy
Dr. Paul Martin Discusses Galgt2 Gene Therapy for Muscular Dystrophy Guest: Paul T. Martin,...
20:31
Dr. Louise Rodino-Klapac Discusses Alpha 7 Integrin As A Therapeutic Approach to Muscular Dystrophy
Dr. Louise Rodino-Klapac Discusses Alpha 7 Integrin As A Therapeutic Approach to Muscular...
09:37
Dr. James Ervasti Discusses Stability of Therapeutic Forms of Dystrophin :: January 2013
Dr. James Ervasti Discusses Stability of Therapeutic Forms of Dystrophin :: January 2013 Guest:...
19:08
Dr. Federica Montanaro Discusses New Cardiac Dystrophin Associated Proteins
Dr. Federica Montanaro Discusses New Cardiac Dystrophin Associated Proteins :: December 2012...
17:56
Professor Francesco Muntoni Discusses Congenital Muscular Dystrophies
Professor Francesco Muntoni Discusses Congenital Muscular Dystrophies Guest: Professor Francesco...
26:30
Dr. Louise Rodino-Klapac Discusses Advances in Dysferlin Gene Therapy
Dr. Louise Rodino-Klapac Discusses Advances in Dysferlin Gene Therapy Guest: Louise...
11:03
Dr. Hugh Allen Discusses Cardiomyopathy in Duchenne Muscular Dystrophy
Dr. Hugh Allen Discusses Cardiomyopathy in Duchenne Muscular Dystrophy Guest: Hugh Allen, MD,...
16:01
Dr. Jerry Mendell Discusses Newborn Screening in Duchenne Muscular Dystrophy
Dr. Jerry Mendell Discusses Newborn Screening in Duchenne Muscular Dystrophy :: April 2012...
19:18
Dr. Thomas Voit Discusses Gamma Sarcoglycan Gene Therapy
Dr. Thomas Voit Discusses Gamma Sarcoglycan Gene Therapy :: March 2012 Guest: Thomas Voit,...
17:43
Dr. Burghes Discusses Antisense Oligomer Treatment in an SMA Mouse Model
Dr. Arthur Burghes discusses antisense oligomer treatment in an SMA mouse model Guest: Arthur...
18:41
Dr. Steve Wilton Discusses Antisense-Induced Exon Skipping
Guest: Professor Steve Wilton, Australian Neuromuscular Research Institute, The University of...
12:54
Dr. Denis Guttridge Discusses NF-kB Therapy for Duchenne Muscular Dystrophy
Guest: Denis Guttridge, PhD, Associate Professor, Molecular Virology, Immunology and Medical...
18:11