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This Month in Muscular Dystrophy

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This Month in Muscular Dystrophy

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Dr. Kevin Flanigan Discusses IRES-Induced Dystrophin as a Potential Therapy for DMD

Guest Host: Scott Harper, PhD, is a principal investigator in the Center for Gene Therapy in The...

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Dr. Scott Harper Discusses RNAi silencing in Limb Girdle Muscular Dystrophy 1A

Guest: Scott Harper, PhD, is a principal investigator in the Center for Gene Therapy in The...

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Dr. Volker Straub Discusses the Use of Muscle MRI in Muscular Dystrophy

Dr. Volker Straub Discusses the Use of Muscle MRI in Muscular Dystrophy Guest: Volker Straub,...

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Dr. Jeff Chamberlain Discusses Gene and Cell Mediated Therapies for Muscular Dystrophy

Dr. Jeff Chamberlain Discusses Gene and Cell Mediated Therapies for Muscular Dystrophy Guest:...

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Dr. Paul Martin Discusses Galgt2 Gene Therapy for Muscular Dystrophy

Dr. Paul Martin Discusses Galgt2 Gene Therapy for Muscular Dystrophy Guest: Paul T. Martin,...

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Dr. James Ervasti Discusses Stability of Therapeutic Forms of Dystrophin :: January 2013

Dr. James Ervasti Discusses Stability of Therapeutic Forms of Dystrophin :: January 2013 Guest:...

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Dr. Federica Montanaro Discusses New Cardiac Dystrophin Associated Proteins

Dr. Federica Montanaro Discusses New Cardiac Dystrophin Associated Proteins :: December 2012...

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Professor Francesco Muntoni Discusses Congenital Muscular Dystrophies

Professor Francesco Muntoni Discusses Congenital Muscular Dystrophies Guest: Professor Francesco...

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Dr. Louise Rodino-Klapac Discusses Advances in Dysferlin Gene Therapy

Dr. Louise Rodino-Klapac Discusses Advances in Dysferlin Gene Therapy Guest: Louise...

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Dr. Hugh Allen Discusses Cardiomyopathy in Duchenne Muscular Dystrophy

Dr. Hugh Allen Discusses Cardiomyopathy in Duchenne Muscular Dystrophy Guest: Hugh Allen, MD,...

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Dr. Jerry Mendell Discusses Newborn Screening in Duchenne Muscular Dystrophy

Dr. Jerry Mendell Discusses Newborn Screening in Duchenne Muscular Dystrophy :: April 2012...

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Dr. Thomas Voit Discusses Gamma Sarcoglycan Gene Therapy

Dr. Thomas Voit Discusses Gamma Sarcoglycan Gene Therapy :: March 2012 Guest: Thomas Voit,...

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Dr. Burghes Discusses Antisense Oligomer Treatment in an SMA Mouse Model

Dr. Arthur Burghes discusses antisense oligomer treatment in an SMA mouse model Guest: Arthur...

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Dr. Steve Wilton Discusses Antisense-Induced Exon Skipping

Guest: Professor Steve Wilton, Australian Neuromuscular Research Institute, The University of...

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Dr. Denis Guttridge Discusses NF-kB Therapy for Duchenne Muscular Dystrophy

Guest: Denis Guttridge, PhD, Associate Professor, Molecular Virology, Immunology and Medical...

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